3 minute lightning oral presentation (and poster) ESA-SRB-APEG-NZSE 2022

The long-acting recombinant human follicle-stimulating hormone (SAFA-FSH) for enhancing spermatogenesis (#109)

Daham Kim 1 , Soohyun Lee 1 , Cheol Ryong Ku 1 , Yoon Hee Cho 1 , Kyungsun Lee 2 , Jaekyu Han 2 , Susan Chi 2 , Moo Young Song 2 , Sang-hoon Cha 2 , Eun Jig Lee 1
  1. Department of Internal Medicine, Yonsei University College of Medicine, Seoul, Korea
  2. Aprilbio Co., LTD., Rm 602, Biomedical Science Building, Kangwon National University, Chuncheon, Korea

It is recommended to replace follicle-stimulating hormone (FSH) in stimulating spermatogenesis in man who are infertile due to secondary hypogonadism whose sperm counts have not responded to human chorionic gonadotropin (hCG) alone. However, FSH have a short serum half-life which requires frequent administration to maintain the therapeutic efficacy. To improve the pharmacokinetic properties, we had developed one of unique albumin-related technology, coined as “anti-serum albumin Fab-associated” (SAFA) technology. We tested the feasibility of applying SAFA technology in creating a long-acting FSH as a therapeutic candidate for secondary hypogonadism patients.

SAFA-FSH was produced in a Chinese hamster ovary (CHO) expression system. To confirm the biological function, production of cyclic AMP and phosphorylation of ERK1/2 and CREB were measured in TM4-FSHR cells. The effect on spermatogenesis in a hypogonadal rat model treated with gonadotropin releasing hormone (GnRH) agonist was investigated.

In cell line experiments, SAFA-FSH treatment increased production of cyclic AMP and increased phosphorylation of ERK1/2 and CREB in a dose dependent manner. In animal experiments, sperm production wasn't restored after hCG alone treatment. However, Sperm production was restored after additional conventional FSH treatment at intervals of 3 times per week or once every 5 days. Further, sperm production was restored even after additional SAFA-FSH treatment at intervals once every 5 days or once every 10 days.

In conclusion, long-acting FSH with bioactivity was successfully created by using SAFA technology. The data support further development of SAFA-FSH in the clinical setting, potentially representing an important advance in treatment of secondary hypogonadism patients.